Rare Disease Recruitment Models Evolving

New technologies and design models are enabling clinical trial sponsors to get creative as they tackle the challenges of rare disease studies.

In this article, ERT’s Susan Dallabrida, PhD, reviews the important role caregivers play in collecting primary and secondary endpoints in rare disease trials and how study designs that include electronic Clinical Outcome Assessments (eCOA) and effective rater training strategies can help sponsors overcome challenges and accelerate rare disease research.

Read the article here.